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EHA 2023 | BEACON trial results: safety & efficacy of bitopertin in adults with EPP

William Savage • 10 Jun 2023
EHA 2023
Erythropoietic Protoporphyria Rare Diseases Bitopertin
BEACON

William Savage, MD, PhD, Disc Medicine, Watertown, MA, shares the results of the Phase II BEACON trial (ACTRN12622000799752) evaluating the safety, tolerability, pharmacokinetics (PK), and efficacy of bitopertin treatment in adults with erythropoietic protoporphyria (EPP). The trial reported a significant reduction in protoporphyrin IX as well as significant improvements in measures of light tolerance. This interview took place at the 28th Congress of the European Hematology Association (EHA) 2023 in Frankfurt, Germany.

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