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The 2022 Tandem Meetings | Gene therapy for Fanconi anemia

Agnieszka Czechowicz • 25 Apr 2022
The 2022 Tandem Meetings
Anemias Rare Diseases

Agnieszka Czechowicz, MD, PhD, Stanford University, Stanford, CA, explains the procedure of gene therapy for Fanconi Anemia. Currently, only patients with the FANCA subtype can be treated with gene therapy. Gene therapy is performed ex vivo using lentiviral vectors. This interview took place at the Transplantation & Cellular Therapy (TCT) Meetings of ASTCT™ and CIBMTR® 2022 in Salt Lake City, Utah.

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