The Community Focus Channel on VJHemOnc is an independent medical education platform, supported with funding from Johnson & Johnson (Gold). Supporters have no influence on the production of content. The levels of sponsorship listed are reflective of the amount of funding given.
The Non-Malignant Channel on VJHemOnc is an independent medical education platform, supported with funding from Agios (Gold). Supporters have no influence on the production of content. The levels of sponsorship listed are reflective of the amount of funding given.
The Sickle Cell Disease Channel on VJHemOnc is an independent medical education platform, supported with funding from Agios (Gold). Supporters have no influence on the production of content. The levels of sponsorship listed are reflective of the amount of funding given.
The Thalassemia Channel on VJHemOnc is an independent medical education platform, supported with funding from Agios (Gold). Supporters have no influence on the production of content. The levels of sponsorship listed are reflective of the amount of funding given.
ESH Erythro 2025 | Promising therapies for SCD & thalassemia: gene therapy, luspatercept, mitapivat & more
In this video, Perla Eleftheriou, MRCP, FRCpath, University College London Hospitals NHS Foundation Trust, London, UK, gives an overview of exciting therapies being explored in sickle cell disease (SCD) and thalassemia, highlighting the recent approval of CRISPR-based gene editing for these diseases and the potential for expanding treatment accessibility. Dr Eleftheriou notes that eligibility remains a challenge for these gene therapies and further discusses the benefits of luspatercept and mitapivat. This interview took place at the 4th ESH Translational Research Conference on Pathophysiology and Clinical Advances in Sickle Cell Disease and Thalassemia in Dublin, Ireland.
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