Adeno-associated virus mediated gene transfer for hemophilia B

Press brief by Katherine A. High, MD of Perelman School of Medicine at the University of Pennsylvania, Philadelphia, PA, on Spk-9001: Adeno-associated virus mediated gene transfer for hemophilia B achieves sustained mean factor IX activity levels of more than 30% without immunosuppression. Recorded at the 2016 American Society of Hematology (ASH) Annual Meeting, held in San Diego, CA.

Share this video